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Antisense oligonucleotides for rescuing splicing mutations in hotspot exons

An antisense oligonucleotide to rescue multiple splicing mutations in hotspot exons Overview Research by William Fairbrother at Brown University centers around a therapeutic use of ASOs to enhance splicing for various mutations using a single ASO. This can allow for the expansion of treatment options for a broader range of patients with the same underlying...

Published: 10/23/2025 | Inventor(s): William Fairbrother, Jeremiah Buerer, Chaorui Duan

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Category(s): Assay, Therapeutics